Rare Diseases SASep 19, 20234 min readOrchard Therapeutics Announces Acceptance of Biologics License Application for OTL-200 in MLD.Hope is on the horizon for patients impacted by metachromatic leukodystrophy.
Rare Diseases SAOct 17, 20222 min readExperimental cancer drug could be effective in treating idiopathic pulmonary fibrosisResearchers have shown that the medication saracatinib shows promise as a treatment for idiopathic pulmonary fibrosis (IPF). Saracatinib...